Hope for Friedreich's ataxia: new drug trial aims to slow disease progression
NCT ID NCT06447025
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study is testing the long-term safety and effectiveness of an experimental drug called CTI-1601 for people with Friedreich's ataxia, a rare genetic disease that affects movement and heart function. It includes about 85 adolescents and adults who have or have not taken the drug before. Participants receive daily injections, and researchers will monitor side effects, heart health, motor skills, and daily living abilities over time.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for FRIEDREICH ATAXIA are added.
By submitting, you agree to our Terms of use
Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
Children's Hospital of the University of Pennsylvania (CHOP)
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Clinilabs Drug Development, Corp.
RECRUITINGEatontown, New Jersey, 07724, United States
-
Fixel Institute for Neurological Disease, University of Florida Health
ACTIVE_NOT_RECRUITINGGainesville, Florida, 32608, United States
-
Morsani Center for Advanced Health Care, University of South Florida Health
RECRUITINGTampa, Florida, 33612, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
Ohio State University United States
ACTIVE_NOT_RECRUITINGColumbus, Ohio, 43210, United States
-
Uncommon Cures
RECRUITINGChevy Chase, Maryland, 20815, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
-
University of California Los Angeles
RECRUITINGLos Angeles, California, 90095, United States
-
University of Iowa
RECRUITINGIowa City, Iowa, 52242, United States