New daily shot aims to slow rare nerve disease
NCT ID NCT06447025
First seen Apr 04, 2026 · Last updated May 07, 2026 · Updated 7 times
Summary
This study is testing the long-term safety and effects of a daily injection called CTI-1601 in people with Friedreich's ataxia, a rare genetic disorder that damages the nervous system. About 85 adults and teens who have or haven't taken the drug before will receive it for an extended period. Researchers will monitor side effects, heart function, movement, and daily living skills to see if the treatment helps control the disease over time.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Children's Hospital of the University of Pennsylvania (CHOP)
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
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Clinilabs Drug Development, Corp.
RECRUITINGEatontown, New Jersey, 07724, United States
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Fixel Institute for Neurological Disease, University of Florida Health
ACTIVE_NOT_RECRUITINGGainesville, Florida, 32608, United States
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Morsani Center for Advanced Health Care, University of South Florida Health
RECRUITINGTampa, Florida, 33612, United States
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Ohio State University United States
ACTIVE_NOT_RECRUITINGColumbus, Ohio, 43210, United States
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Uncommon Cures
RECRUITINGChevy Chase, Maryland, 20815, United States
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University of California Los Angeles
RECRUITINGLos Angeles, California, 90095, United States
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University of Iowa
RECRUITINGIowa City, Iowa, 52242, United States
Conditions
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