Hope for Friedreich's ataxia: new drug trial aims to slow disease progression
Disease control
Recruiting now
This study is testing the long-term safety and effectiveness of an experimental drug called CTI-1601 for people with Friedreich's ataxia, a rare genetic disease that affects movement and heart function. It includes about 85 adolescents and adults who have or have not taken the dr…
Phase: PHASE2 • Sponsor: Larimar Therapeutics, Inc. • Aim: Disease control
Last updated Jun 27, 2026 12:34 UTC