Terminated trial tests First-of-its-Kind treatment for kids with rare nerve disease
Disease control
Terminated
This study aimed to test the safety of a new drug called nomlabofusp in children and teenagers with Friedreich's ataxia, a rare genetic disorder that damages the nervous system. The trial was small, involving about 18 participants, and was designed to see how their bodies handled…
Phase: PHASE1 • Sponsor: Larimar Therapeutics, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:35 UTC