New daily shot aims to slow rare nerve disease
Disease control
Recruiting now
This study is testing the long-term safety and effects of a daily injection called CTI-1601 in people with Friedreich's ataxia, a rare genetic disorder that damages the nervous system. About 85 adults and teens who have or haven't taken the drug before will receive it for an exte…
Phase: PHASE2 • Sponsor: Larimar Therapeutics, Inc. • Aim: Disease control
Last updated May 07, 2026 18:43 UTC