The Children's Hospital Of Zhejiang University School Of Medicine

This study tests whether adding the drug selinexor to standard chemotherapy can help children with a rare, high-risk form of acute myeloid leukemia (AML) called NUP98-positive. The trial will enroll 10 children and measure how many achieve complete remission. The goal is to impro…

This early-stage study tests a gene therapy called AAV9.hMCOLN1co in one child with Mucolipidosis Type IV, a rare genetic disorder. The goal is to see if the treatment is safe and can help control the disease. Participants must be between 1.5 and 8 years old and have a confirmed …

This early-stage study tests whether a special type of immune cell, called a CAR-T cell, is safe for people with severe lupus that hasn't responded to standard treatments. The cells are designed to target and destroy faulty immune cells that cause lupus. The study includes 22 par…

This study aims to create an intelligent ultrasound system that can automatically identify different types of neuroblastoma tumors in children. Researchers will use ultrasound images and medical records from 300 children to train the AI to predict tumor type, risk level, and trea…