Biogen

This study compares two drugs, diroximel fumarate and dimethyl fumarate, with an existing treatment (fingolimod) in children with relapsing multiple sclerosis. About 185 kids will take the drugs for up to 4 years to check safety and how well they prevent relapses and brain lesion…

This study tests a drug called salanersen in babies with spinal muscular atrophy (SMA) who already received gene therapy. The goal is to see if adding salanersen is safe and helps improve muscle function. About 42 infants with two copies of the SMN2 gene will take part. The study…