SPINAL MUSCULAR ATROPHY
Clinical trials for SPINAL MUSCULAR ATROPHY explained in plain language.
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New implant could end painful spinal injections for SMA patients
Disease control Recruiting nowThis study tests a device called ThecaFlex DRx that is implanted under the skin to deliver the SMA drug nusinersen directly into the spinal fluid. It is for people with spinal muscular atrophy who have trouble with repeated spinal injections. The goal is to see if the device work…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Alcyone Therapeutics, Inc • Aim: Disease control
Last updated May 26, 2026 03:34 UTC
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Once-a-Year shot could help SMA patients move better
Disease control Recruiting nowThis study tests a new drug called salanersen (BIIB115) in people aged 15 to 60 with spinal muscular atrophy (SMA). The drug aims to help the body produce more of a key protein needed for muscle and nerve function. Participants receive one injection into the spinal fluid each yea…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE3 • Sponsor: Biogen • Aim: Disease control
Last updated May 26, 2026 03:34 UTC
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New hope for SMA babies: drug trial aims to boost motor milestones
Disease control Recruiting nowThis study tests a drug called apitegromab in babies under 2 years old who have spinal muscular atrophy (SMA), a condition that weakens muscles. The goal is to see if the drug helps improve movement skills like rolling, sitting, and crawling. All participants must already be on s…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE2 • Sponsor: Scholar Rock, Inc. • Aim: Disease control
Last updated May 22, 2026 13:55 UTC
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Could electrical shocks help weak muscles? new study hopes to find out
Symptom relief Recruiting nowThis study is testing whether whole-body electrical muscle stimulation (WB-EMS) can help adults with neuromuscular diseases like ALS, muscular dystrophy, and myasthenia gravis exercise safely. Because these conditions make normal exercise difficult, WB-EMS uses electrical pulses …
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: University of Missouri-Columbia • Aim: Symptom relief
Last updated May 26, 2026 03:30 UTC
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SMA treatments reveal new disease patterns – scientists investigate
Knowledge-focused Recruiting nowThis study follows 60 children with spinal muscular atrophy (SMA) who are already receiving SMN-restoring therapies like nusinersen or gene therapy. Researchers want to describe the new disease patterns that emerge with these treatments and find better ways to monitor progress. T…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Hospices Civils de Lyon • Aim: Knowledge-focused
Last updated May 26, 2026 03:37 UTC
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Spanish SMA study aims to standardize patient data collection
Knowledge-focused Recruiting nowThis study will follow up to 1,000 people with spinal muscular atrophy (SMA) in Spain over many years to see how their motor skills and health change in real life. Researchers will collect information from routine doctor visits, including tests of movement and breathing support. …
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: Fundació Sant Joan de Déu • Aim: Knowledge-focused
Last updated May 26, 2026 03:34 UTC
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New study peers inside muscles of kids with SMA to see how drugs really work
Knowledge-focused Recruiting nowThis study watches children and teens with spinal muscular atrophy (SMA) who are already taking approved treatments. Researchers use MRI scans, strength tests, and blood samples to see how muscles and nerves respond over 12 months. The goal is to better understand the disease and…
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: St. Jude Children's Research Hospital • Aim: Knowledge-focused
Last updated May 26, 2026 03:31 UTC
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New study tracks daily fatigue in SMA patients on standard treatment
Knowledge-focused Recruiting nowThis study aims to better understand physical tiredness in people with spinal muscular atrophy (SMA) who are already taking the medication nusinersen. Researchers will use a new questionnaire called the SMA EFFORT to measure how fatigue affects daily activities. About 45 adolesce…
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: Columbia University • Aim: Knowledge-focused
Last updated May 26, 2026 03:31 UTC