MYOTONIC DYSTROPHY 1
Clinical trials for MYOTONIC DYSTROPHY 1 explained in plain language.
Never miss a new study
Get alerted when new MYOTONIC DYSTROPHY 1 trials appear
Sign up with your email to follow new studies for MYOTONIC DYSTROPHY 1, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
Drug trial tests hope for debilitating muscle disease in teens and adults
Disease control CompletedThis study tested whether a drug called Tideglusib is safe and helpful for adolescents and adults with a severe, early-onset form of myotonic dystrophy, a genetic muscle-wasting disease. Sixteen participants aged 12 to 45 took the drug to see if it could improve muscle function, …
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE2 • Sponsor: AMO Pharma Limited • Aim: Disease control
Last updated Apr 04, 2026 00:21 UTC
-
First human trial tests potential new treatment for rare muscle disease
Disease control CompletedThis study tested the safety and effects of a new drug called AOC 1001 in adults with myotonic dystrophy type 1, a genetic muscle-wasting disease. Thirty-nine participants received either the drug or a placebo through an IV to see how their bodies handled it and if it affected th…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE1, PHASE2 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Apr 01, 2026 14:41 UTC
-
Extended trial tests promising drug for genetic muscle disease
Disease control CompletedThis study continued testing an experimental drug called AOC 1001 in adults with myotonic dystrophy type 1, a genetic muscle-wasting disease. It followed 37 participants from a previous trial to check long-term safety and see if the drug continues to work when given every 8 weeks…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE2 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:32 UTC
-
First human test of potential muscle disease treatment
Disease control CompletedThis early-stage study tested the safety of a new drug called PGN-EDODM1 in 24 adults with Myotonic Dystrophy Type 1 (DM1), a genetic muscle-wasting disease. The main goal was to see if single doses given through an IV were safe and well-tolerated. Researchers also measured how t…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE1 • Sponsor: PepGen Inc • Aim: Disease control
Last updated Mar 27, 2026 12:38 UTC
-
Researchers probe deadly blood clot mystery in muscle disease
Knowledge-focused CompletedThis study aims to understand why people with myotonic dystrophy type 1 (DM1) have a much higher risk of dangerous blood clots in their veins. Researchers will test the blood of 100 DM1 patients and 30 healthy volunteers to look for clotting abnormalities and analyze gene activit…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: NA • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Knowledge-focused
Last updated Apr 03, 2026 14:41 UTC