MYOTONIC DYSTROPHY 1
Clinical trials for MYOTONIC DYSTROPHY 1 explained in plain language.
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Major trial tests new IV drug for debilitating muscle disease
Disease control OngoingThis study is testing whether an intravenous drug called AOC 1001 can improve muscle function and control symptoms in adults with myotonic dystrophy type 1 (DM1). Participants receive either the drug or a placebo via infusion every 8 weeks for about a year. The main goal is to se…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE3 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Apr 03, 2026 14:41 UTC
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Four-Year trial tests potential new treatment for debilitating muscle disease
Disease control ENROLLING_BY_INVITATIONThis study is testing the long-term safety and effectiveness of an investigational drug called del-desiran for adults with myotonic dystrophy type 1 (DM1), a genetic muscle-wasting disease. Participants who completed a previous related study will receive an intravenous infusion o…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE3 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:28 UTC
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Scientists map the journey of a rare muscle disease
Knowledge-focused ENROLLING_BY_INVITATIONThis study aims to better understand Myotonic Dystrophy Type 1 (DM1) in Chinese patients by observing how the disease progresses over time. Researchers will follow 500 adult patients, collecting detailed health information through tests, scans, and questionnaires. The goal is to …
Matched conditions: MYOTONIC DYSTROPHY 1
Sponsor: Huashan Hospital • Aim: Knowledge-focused
Last updated Mar 30, 2026 14:34 UTC