MYOTONIC DYSTROPHY 1
Clinical trials for MYOTONIC DYSTROPHY 1 explained in plain language.
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New drug trial aims to tame muscle stiffness in rare disease
Disease control Recruiting nowThis study tests an experimental drug called PGN-EDODM1 in 24 adults with myotonic dystrophy type 1 (DM1), a condition that causes muscle stiffness and weakness. The main goal is to see if the drug is safe and tolerable compared to a placebo. Researchers will also measure how the…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE2 • Sponsor: PepGen Inc • Aim: Disease control
Last updated May 26, 2026 04:58 UTC
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New hope for muscle disease: experimental drug ARO-DM1 enters human trials
Disease control Recruiting nowThis study tests an experimental drug called ARO-DM1 in adults aged 18 to 65 with type 1 myotonic dystrophy, a genetic muscle disorder. The goal is to check the drug's safety and how the body processes it. Participants receive either the drug or a placebo, and the study involves …
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE1, PHASE2 • Sponsor: Arrowhead Pharmaceuticals • Aim: Disease control
Last updated May 22, 2026 14:05 UTC
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Hope for DM1: Long-Term safety trial launches for experimental drug
Disease control Recruiting nowThis study looks at the long-term safety of an experimental drug called PGN-EDODM1 for people with myotonic dystrophy type 1 (DM1). It is for those who have already taken the drug in a previous study. About 48 adults will take part, and researchers will track any side effects ove…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE2 • Sponsor: PepGen Inc • Aim: Disease control
Last updated May 18, 2026 12:07 UTC
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New drug ATX-01 targets muscle stiffness in rare disease
Disease control Recruiting nowThis early-stage trial tests a new drug, ATX-01, in 56 adults aged 18 to 64 with myotonic dystrophy type 1 (DM1), a condition causing muscle stiffness and weakness. The main goal is to see if ATX-01 is safe and tolerable compared to a placebo. Participants will receive either one…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE1, PHASE2 • Sponsor: ARTHEx Biotech S.L. • Aim: Disease control
Last updated May 14, 2026 12:04 UTC
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Could a common diabetes drug ease muscle symptoms in Steinert's disease?
Symptom relief Recruiting nowThis phase 3 trial tests whether metformin, a common diabetes drug, can improve muscle function in adults with myotonic dystrophy type 1 (Steinert's disease). About 142 non-diabetic participants will receive either metformin or a placebo for 6 months. The study measures changes i…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE3 • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Symptom relief
Last updated May 26, 2026 04:57 UTC
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Spain launches massive DM1 registry to unlock disease secrets
Knowledge-focused Recruiting nowThis study aims to create a comprehensive national registry for Myotonic Dystrophy Type 1 (DM1) in Spain, collecting clinical, genetic, and protein data from 3,000 participants. By gathering detailed information, researchers hope to better understand the disease and identify peop…
Matched conditions: MYOTONIC DYSTROPHY 1
Sponsor: Fundació Institut Germans Trias i Pujol • Aim: Knowledge-focused
Last updated May 20, 2026 11:55 UTC