New shot takes aim at genetic high cholesterol

NCT ID NCT07465263

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This Phase 3 trial tests an injection called SYH2053 for people with heterozygous familial hypercholesterolemia (HeFH), a genetic condition causing very high LDL cholesterol. About 135 adults on stable statin therapy will receive either the drug or a placebo. The main goal is to see how much LDL cholesterol drops after about 11 months.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

SYH2053 injection

What this could lead to

If successful, this could provide a new treatment option to lower LDL cholesterol in people with HeFH, potentially reducing their risk of heart disease.

What could go wrong

This is a Phase 3 trial, but it is not yet recruiting and only includes 135 participants. The drug may not lower cholesterol enough or could have side effects. Results may not apply to all HeFH patients.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

familial hypercholesterolemia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••