New stem cell approach could help more sickle cell patients

NCT ID NCT03121001

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This phase II trial is testing a stem cell transplant from a half-matched donor for people with severe sickle cell disease. Participants receive chemotherapy, radiation, and immune-suppressing drugs before the transplant to help the new cells take hold. The main goal is to see if the donor stem cells successfully engraft by day 60, which could lead to better disease control.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

stem cell transplant from a half-matched donor

What this could lead to

If successful, this approach could offer a way to control severe sickle cell disease using a donor who is only half-matched, making transplants available to more patients.

What could go wrong

This is an early phase II trial with only 50 participants, so results may not apply broadly. The transplant carries risks like graft failure, infection, and side effects from chemotherapy and radiation.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

sickle cell disease

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • University of Illinois at Chicago

    RECRUITING

    Chicago, Illinois, 60612, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••