Can a biomarker predict who responds to a new AML combo?

NCT ID NCT02583893

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This phase 2 trial tested whether certain biomarkers in bone marrow can predict how well patients with high-risk acute myeloid leukemia (AML) respond to treatment with sirolimus plus standard chemotherapy (MEC). The study enrolled 39 adults with AML that was hard to treat or had come back. Researchers measured changes in a protein called pS6 in bone marrow samples to see if it could forecast remission. The goal was to find a way to personalize treatment for this aggressive cancer.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Sirolimus (Rapamycin) combined with chemotherapy (Mitoxantrone, Etoposide, Cytarabine)

What this could lead to

If successful, this could help doctors predict which high-risk AML patients will respond to sirolimus plus chemotherapy, leading to more personalized treatment.

What could go wrong

This is a small, early-phase study (39 patients) focused on biomarkers, not a direct test of a new cure. The results may not apply to all AML patients, and the chemotherapy has significant side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

acute myeloid leukemia therapy related acute myeloid leukemia and myelodysplastic syndrome

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Thomas Jefferson University

    Philadelphia, Pennsylvania, 19107, United States