New drug shows promise for rare fat disorder in small trial

NCT ID NCT04159415

First seen Nov 17, 2025 · Last updated May 12, 2026 · Updated 20 times

Summary

This study tested a new drug called REGN4461 in 16 people with generalized lipodystrophy, a rare condition where the body lacks fat tissue, leading to severe metabolic problems like high blood sugar and high triglycerides. The drug aims to mimic a natural hormone (leptin) to improve these levels. Results focused on changes in blood sugar and fat levels after 8 weeks of treatment.

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Contacts and locations

Locations

  • Regeneron Research Site

    Bethesda, Maryland, 20892, United States

  • Regeneron Research Site

    Ann Arbor, Michigan, 48105, United States

  • Regeneron Research Site

    Dallas, Texas, 75390, United States

  • Regeneron Research Site

    Piura, 2665, Peru

  • Regeneron Research Site

    Moscow, 117036, Russia

  • Regeneron Research Site

    Ankara, 06230, Turkey (Türkiye)

  • Regeneron Research Site

    Diyarbakır, 21808, Turkey (Türkiye)

  • Regeneron Research Site

    Izmir, 35100, Turkey (Türkiye)

Conditions

Explore the condition pages connected to this study.