New hope for youngest kids with rare fat disorder
NCT ID NCT06502990
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests a drug called metreleptin in 15 children under 6 years old who have a rare disease called generalized lipodystrophy, which prevents the body from storing fat properly and often leads to diabetes and high triglycerides. The goal is to see if the drug can lower blood fats and improve blood sugar control. All children will receive the drug, and researchers will monitor safety and effectiveness for 12 months.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Assistance Publique-Hopitaux de Paris (AP-HP) - Hopital Universitaire Robert-Debre
RECRUITINGParis, France
Contact
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Azienda Ospedaliera Universitaria "Federico II"
RECRUITINGNaples, 80131, Italy
Contact
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Azienda Ospedaliero Universitaria Maggiore della Carità di Novara
RECRUITINGNovara, 28100, Italy
Contact
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Azienda Ospedaliero Universitaria Pisana
RECRUITINGPisa, 56124, Italy
Contact
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Azienda Ospedaliero-Universitaria di Parma
RECRUITINGParma, 43126, Italy
Contact
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Hôpital Necker - Enfants Malades
RECRUITINGParis, 75015, France
Contact
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IRCCS Ospedale Pediatrico Bambino Gesù
RECRUITINGChieti, 66100, Italy
Contact
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IRCCS Ospedale Pediatrico Bambino Gesù
RECRUITINGRome, 00165, Italy
Contact
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Ospedale Filippo Del Ponte Varese - ASST Sette Laghi
RECRUITINGVarese, 21100, Italy
Contact
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UZ Leuven
RECRUITINGLeuven, 3000, Belgium
Contact
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Universitaetsklinikum Ulm - Klinik fuer Kinder- und Jugendmedizin
RECRUITINGUlm, 89075, Germany
Contact
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Universitätsklinikum Hamburg-Eppendorf
NOT_YET_RECRUITINGHamburg, 20251, Germany
Contact