Drug shows promise for rare disease Survivors' daily struggles
NCT ID NCT04977388
First seen Nov 01, 2025 · Last updated Apr 24, 2026 · Updated 20 times
Summary
This study tested whether the drug Northera (droxidopa) is safe and helpful for adults with Menkes disease or Occipital Horn Syndrome who experience low blood pressure and other nervous system symptoms. Three participants took either the drug or a placebo in a crossover design. The goal was to see if the drug could improve blood pressure stability and daily life without serious side effects.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Vagelos College of Physicians and Surgeons, Columbia University
New York, New York, 10032, United States
Conditions
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