Could a blood pressure drug improve daily life for rare disease survivors?

This study tested whether the drug Northera (droxidopa) is safe and helpful for adults with Menkes disease or Occipital Horn Syndrome who have trouble with low blood pressure and other symptoms of dysautonomia. Three participants took either the drug or a placebo in a crossover design to compare effects. The goal was to see if the drug could improve blood pressure and make daily activities easier.