New hope for rare copper deficiency: lifesaving treatment now available for young children

NCT ID NCT04074512

First seen Nov 12, 2025 · Last updated May 02, 2026 · Updated 22 times

Summary

This program provides copper histidinate injections under the skin for children under 6 with Menkes disease, a rare genetic condition that prevents the body from using copper properly. The treatment aims to supply the copper the body needs to slow disease progression. It is available to newly diagnosed patients or those who previously participated in a related study.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Children's Hospital of Pittsburgh

    Pittsburgh, Pennsylvania, 15224, United States

  • Connecticut Children's Medical Center

    Hartford, Connecticut, 06106, United States

  • Cook Children's Health Care System

    Fort Worth, Texas, 76104, United States

  • Duke University Hospital

    Durham, North Carolina, 27710, United States

  • Emory University

    Atlanta, Georgia, 30322, United States

  • Helen DeVos Children's Hospital

    Grand Rapids, Michigan, 49503, United States

  • Johns Hopkins All Children's Hospital

    St. Petersburg, Florida, 33701, United States

  • Lurie Children's Hospital of Chicago

    Chicago, Illinois, 60611, United States

  • Maine Medical Center

    Portland, Maine, 04102, United States

  • Memorial Healthcare Systems

    Hollywood, Florida, 33021, United States

  • Monroe Carrell Jr. Children's Hospital at Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States

  • Oregon Health & Science University

    Portland, Oregon, 97239, United States

  • Phoenix Children's Hospital

    Phoenix, Arizona, 85016, United States

  • Rady Children's Hospital

    San Diego, California, 92123, United States

  • Seattle Children's Hospital

    Seattle, Washington, 98105, United States

  • Shodair Children's Hospital

    Helena, Montana, 59601, United States

  • University of California Davis Medical Center

    Sacramento, California, 95817, United States

  • University of Iowa Stead Family Children's Hospital

    Iowa City, Iowa, 52242, United States

Conditions

Explore the condition pages connected to this study.