New hope for rare anemia patients: drug may cut transfusions by a third

NCT ID NCT07331818

First seen Jan 12, 2026 · Last updated Apr 29, 2026 · Updated 16 times

Summary

This study tests a drug called luspatercept in 45 people with rare inherited anemias that cause low red blood cells. The goal is to see if it can reduce the need for blood transfusions by at least one third in those who rely on transfusions, or raise hemoglobin levels in those who don't. Participants will receive the drug and be monitored for 12 weeks to measure these changes.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Assistance Publique Hôpitaux de Paris - Hôpital Necker

    Paris, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Assistance Publique Hôpitaux de Paris - Hôpital Saint-Louis

    Paris, 75010, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • CHU Bordeaux-Hôpital Haut-Lévêque

    Pessac, 33600, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Centre Hospitalier Universitaire de Montpellier

    Montpellier, 34295, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano

    Milan, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • GCS Groupement des Hôpitaux de l'Institut Catholique de Lille

    Lille, 59800, France

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.