Could a cancer pill stop debilitating nosebleeds? new trial hopes so.

NCT ID NCT03850964

First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study tests whether a low dose of pazopanib, a drug currently used for cancer, can reduce severe nosebleeds and improve anemia in people with hereditary hemorrhagic telangiectasia (HHT). About 70 participants will take either the drug or a placebo daily for 24 weeks. Researchers will measure nosebleed duration and blood counts to see if the drug helps control the disease.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

pazopanib (a low-dose cancer drug repurposed for HHT)

What this could lead to

If it works, this could offer a new daily pill to control severe nosebleeds and anemia in people with HHT, reducing the need for transfusions.

What could go wrong

This is a mid-stage trial with only 70 participants, so results may not apply to everyone. Pazopanib has side effects like high blood pressure and liver issues, and the placebo comparison means the real benefit is still uncertain.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

anemia Epistaxis hereditary hemorrhagic telangiectasia telangiectasia, hereditary hemorrhagic, type 1

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Augusta University

    Augusta, Georgia, 30912, United States

  • Cleveland Clinic

    Cleveland, Ohio, 44195, United States

  • John Hopkins University

    Baltimore, Maryland, 21287, United States

  • Massachusetts General Hospital

    Boston, Massachusetts, 02114, United States

  • Mayo Clinic

    Rochester, Minnesota, 55905, United States

  • University of California - Los Angeles

    Los Angeles, California, 90095, United States

  • University of Colorado

    Denver, Colorado, 80045, United States

  • University of North Carolina

    Chapel Hill, North Carolina, 27514, United States

  • University of Texas - Southwestern

    Dallas, Texas, 75390, United States

  • University of Utah Medical Center

    Salt Lake City, Utah, 84132, United States

  • Washington University

    St Louis, Missouri, 63110, United States