15-Year checkup: how did early fabry treatment hold up?
NCT ID NCT04002531
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study checked in on 5 adults with Fabry disease who had been taking enzyme replacement therapy (ERT) since childhood for about 15 years. Researchers measured kidney function and heart health to see how well the long-term treatment worked. The goal was to gather follow-up data, not to test a new treatment.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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Baylor University Medical Center
Dallas, Texas, 75246, United States
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