Researchers peek inside livers after gene therapy for hemophilia

NCT ID NCT05932914

First seen Nov 01, 2025 · Last updated Jun 13, 2026 · Updated 37 times

Summary

This study looks at liver tissue from adults with hemophilia A or B who received gene therapy at least 6 months ago. Researchers want to see how the gene therapy affects liver cells over time. About 8 participants will have a liver biopsy to check for signs of damage and how many cells still carry the therapy.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • St. Jude Children's Research Hospital

    Memphis, Tennessee, 38105, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.