Could a cancer drug help kids with autism speak better?

NCT ID NCT02839915

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tests whether folinic acid (leucovorin), a drug already used to reduce side effects from chemotherapy, can improve language skills in children with autism spectrum disorder. Researchers will give the drug or a placebo to 56 children aged 5 to 17 for 12 to 24 weeks and measure changes in language tests. The goal is to see if this drug can help with a core challenge of autism.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

folinic acid (leucovorin)

What this could lead to

If it works, this could point toward a treatment to improve language skills in children with autism.

What could go wrong

This is a small, early-phase trial with only 56 participants. The drug is not proven for this use, and results may not apply to all children with autism.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

autism spectrum disorder language disorder

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Children's Healtcare of Atlanta

    Atlanta, Georgia, 30322, United States

  • Harvard University

    Lexington, Massachusetts, 02421, United States

  • Southwestern Research and Resource Center

    Phoenix, Arizona, 85016, United States

  • State University of New York, Downstate

    Brooklyn, New York, 11203, United States