Experimental drug aims to stop rare heart disease
NCT ID NCT03702829
First seen Feb 20, 2026 · Last updated May 25, 2026 · Updated 13 times
Summary
This study tested a drug called inotersen in 31 people with a rare condition where a protein builds up in the heart, causing damage. The drug is designed to lower the amount of that protein made by the liver. The goal was to see if it could slow or stop the heart disease, but the study was stopped early.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Brigham and Women's Hospital
Boston, Massachusetts, 02115, United States
Conditions
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