Brain gene therapy tested for Parkinson's – early results in

NCT ID NCT05603312

First seen Jun 26, 2026 · Last updated Jun 26, 2026

Summary

This early-stage trial tested a gene therapy for Parkinson's disease. The treatment involved delivering a gene called GAD into a brain region that controls movement. Only 14 people took part, and the main goal was to check safety, not whether it works. The study is now complete.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

AAV-GAD (gene therapy)

What this could lead to

If successful, this could point toward a new way to control Parkinson's symptoms by delivering a gene that helps calm overactive brain signals.

What could go wrong

This was a very small, early-phase trial focused on safety, not effectiveness. The gene therapy requires brain surgery, which carries risks like infection or bleeding. It may not improve symptoms.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Parkinson disease

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Columbia University Irving Medical Center

    New York, New York, 10032, United States

  • Henry Ford West Bloomfield Hospital

    West Bloomfield, Michigan, 48322, United States

  • Thomas Jefferson University

    Philadelphia, Pennsylvania, 19107, United States

  • Weill Cornell Medicine

    New York, New York, 10021, United States

  • West Virginia University

    Morgantown, West Virginia, 26506, United States

  • Yale University - Yale New Haven Hospital

    New Haven, Connecticut, 06510, United States