One-Time gene shot could free hemophilia b patients from frequent infusions
NCT ID NCT05203679
First seen Apr 03, 2026 · Last updated Apr 25, 2026 · Updated 2 times
Summary
This study tests a one-time gene therapy (BBM-H901) for adults with severe hemophilia B, a bleeding disorder caused by low clotting factor IX. The treatment uses a harmless virus to deliver a working gene, helping the body produce its own clotting factor. The goal is to reduce or prevent bleeding episodes and the need for regular factor infusions. The trial involves 32 participants and is in Phase 2/3.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Anhui Provincial Hospital
Hefei, Anhui, 230022, China
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Henan Cancer Hospital
Zhengzhou, Henan, 450003, China
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Institute of Hematology & Blood Diseases Hospital Chinese Academy of Medical Sciences & Peking Union Medical College
Tianjin, Tianjin Municipality, 300020, China
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Nanfang Hospital Southern Medical University
Guangzhou, Guangdong, 510515, China
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North China University of Science and Technology Affiliated Hospital
Tangshan, Hebei, 063000, China
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Peking Union Medical College Hospital
Beijing, Beijing Municipality, 100005, China
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The Second Hospital of Shanxi Medical University
Taiyuan, Shanxi, 030001, China
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The Second People's Hospital of Shenzhen
Shenzhen, Guangdong, 518025, China
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The second Affiliated Hospital of Kunming Medical University
Kunming, Yunnan, 650032, China
Conditions
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