Gene therapy could free Beta-Thalassemia patients from lifelong transfusions
NCT ID NCT06308159
First seen Jan 04, 2026 · Last updated May 13, 2026 · Updated 22 times
Summary
This study tests a new gene therapy for people with a severe form of beta-thalassemia who need frequent blood transfusions. The treatment involves taking the patient's own blood stem cells, adding a working gene to help them produce healthy hemoglobin, and returning them to the body. The goal is to see if this can safely reduce or eliminate the need for regular transfusions. The study is currently recruiting 6 participants.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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920th Hospital of Joint Logistics Support Force of People's Liberation Army of China
RECRUITINGKunming, Yunnan, 650100, China
Contact Email: •••••@•••••
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Kunming Hope of Health Hospital
RECRUITINGKunming, Yunnan, 650200, China
Contact Email: •••••@•••••
Conditions
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