Lantu Biopharma
Clinical trials sponsored by Lantu Biopharma, explained in plain language.
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Gene therapy hope for SMA patients in low-income countries
Disease control Recruiting nowThis study is testing a gene therapy called vesemnogene lantuparvovec for people with spinal muscular atrophy (SMA) in low- and middle-income countries. The goal is to see how well it works and how safe it is in everyday medical practice. About 15 participants will be followed fo…
Phase: PHASE3 • Sponsor: Lantu Biopharma • Aim: Disease control
Last updated May 17, 2026 06:47 UTC
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Gene therapy could free Beta-Thalassemia patients from lifelong transfusions
Disease control Recruiting nowThis study tests a new gene therapy for people with a severe form of beta-thalassemia who need frequent blood transfusions. The treatment involves taking the patient's own blood stem cells, adding a working gene to help them produce healthy hemoglobin, and returning them to the b…
Phase: PHASE1, PHASE2 • Sponsor: Lantu Biopharma • Aim: Disease control
Last updated May 13, 2026 16:02 UTC