New targeted drug shows promise for rare bile duct cancer

NCT ID NCT05727176

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This Phase 2 trial is testing two doses (20 mg and 16 mg) of the oral drug futibatinib in 120 people with advanced bile duct cancer that has specific FGFR2 gene changes. Participants must have already tried standard chemotherapy. The study aims to see which dose works better at shrinking tumors and controlling the disease, while also checking safety. It is currently recruiting at multiple sites worldwide.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Futibatinib (TAS-120), an oral targeted therapy

What this could lead to

If successful, this could confirm a new standard dose for futibatinib and offer a treatment option for people with advanced bile duct cancer that has FGFR2 gene changes.

What could go wrong

This is a Phase 2 trial with only 120 participants, so results are still early. The drug may not work for everyone, and side effects like high phosphate levels or eye issues are possible.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

cholangiocarcinoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • AOUI Verona - Ospedale Borgo Roma

    RECRUITING

    Verona, 37134, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Alfred Health, Medical Oncology Unit, Second floor William Buckland Radiotherapy Center

    RECRUITING

    Melbourne, Victoria, 3004, Australia

    Contact

  • CEMIC

    RECRUITING

    CABA, 1431, Argentina

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • CHA Bundang Medical Center

    RECRUITING

    Seongnam, 13532, South Korea

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Center for Oncology and Blood Disorders

    WITHDRAWN

    Houston, Texas, 77030, United States

  • Centro Hospitalar Lisboa Norte CHLN EPE - Hospital de Santa Maria

    WITHDRAWN

    Lisbon, 1649-035, Portugal

  • Centrum Onkologii Ziemi Lubelskiej im. w. Jana z Dukli

    WITHDRAWN

    Lublin, 20-0920, Poland

  • Centrum Onkologii-Instytut im. Marii Skłodowskiej - Curie

    RECRUITING

    Warsaw, 02-034, Poland

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Clinica Universidad de Navarra

    RECRUITING

    Pamplona, 31008, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Clinica Universidad de Navarra, Medical Oncology Service (Mariano Ponz Sarvise)

    RECRUITING

    Madrid, 28027, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Dong-A University Hospital

    WITHDRAWN

    Busan, 49201, South Korea

  • Europejskie Centrum Zdrowia Otwock Sp. Z.o.o.

    RECRUITING

    Otwock, 05-400, Poland

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Fundacao Antonio Prudente - A.C.Camargo Cancer Center

    RECRUITING

    São Paulo, 01508-010, Brazil

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Fundação Champalimaud

    WITHDRAWN

    Lisbon, 1400-038, Portugal

  • Gabrail Cancer Center Research

    WITHDRAWN

    Canton, Ohio, 44718, United States

  • Grand River Hospital - Grand River Regional Cancer Centre (GRRCC)

    RECRUITING

    Kitchener, OH, N2G 1G3, Canada

  • Guangdong Provincial People's Hospitall

    RECRUITING

    Guangzhou, Guangdong, 510080, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Gyeongsang National University Hospital

    WITHDRAWN

    Jinju, 52727, South Korea

  • Harbin Medical University - Cancer Hospital

    RECRUITING

    Harbin, Heilongjiang, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Henry Ford Health System

    RECRUITING

    Detroit, Michigan, 48202, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hospital Britanico

    RECRUITING

    Buenos Aires, AEB1280, Argentina

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hospital Erasto Gaertner

    RECRUITING

    Curitiba, 81520-060, Brazil

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hospital General Universitario Gregorio Maranon

    RECRUITING

    Madrid, 28007, Spain

    Contact Phone: •••-•••-••••

    Contact

  • Hospital Universitario 12 de octubre

    RECRUITING

    Madrid, 28043, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hospital Universitario Fundación Jimenez Díaz

    RECRUITING

    Madrid, 28040, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hospital Vall d'Hebron

    RECRUITING

    Barcelona, 08035, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hospital de Base de Sao Jose do Rio Preto

    RECRUITING

    São José do Rio Preto, 15090-000, Brazil

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • IOP - Instituto de Oncologia do Parana

    RECRUITING

    Curitiba, 80530-010, Brazil

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • IRCCS Humanitas Research Hospital

    RECRUITING

    Rozzano, 20089, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Inje University Haeundae Paik Hospital

    RECRUITING

    Busan, 48108, South Korea

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Institut Català d'Oncologia de l'Hospitalet de Llobregat - Hospital Duran i Reynals

    RECRUITING

    Barcelona, 08908, Spain

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Instituto do Cancer do Estado de Sao Paulo

    RECRUITING

    Cerqueira César, 01246-000, Brazil

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Jiangsu Provance Hospital

    RECRUITING

    Nanjing, Jiangsu, 212028, China

  • Jilin Cancer Hospital

    RECRUITING

    Changchun, Jilin, 130028, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Kyungpook National University Hospital

    WITHDRAWN

    Daegu, 41944, South Korea

  • McGill University Health Center

    RECRUITING

    Montreal, Quebec, H4A 3J1, Canada

  • Nagasaki University Hospital

    WITHDRAWN

    Nagasaki, 852-8501, Japan

  • Nagoya University Hospital

    RECRUITING

    Nagoya, 466-8560, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • National Cancer Center Hospital East

    RECRUITING

    Kashiwa-Shi, 277-0882, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Osaka Metropolitan University Hospital

    RECRUITING

    Osaka-Fu, 558-8585, Japan

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Policlinico S. Orsola-Malpighi

    RECRUITING

    Bologna, 40138, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Sanatorio de la Mujer

    WITHDRAWN

    Rosario, S2013, Argentina

  • Shandong University - Shandong Cancer Hospital

    RECRUITING

    Jinan, Shandong, 250117, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Shanghai Gobroad Cancer Hospital China Pharmaceutical University

    RECRUITING

    Shanghai, 200123, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Sir Run Run Shaw Hospital, Zhejiang University

    RECRUITING

    Hangzhou, Zhejiang, 310016, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • St John of God Subiaco Hospital

    RECRUITING

    Subiaco, Western Australia, 6008, Australia

  • St Vincent's Hospital Sydney - The Kinghorn Cancer Centre

    RECRUITING

    Sydney, New South Wales, 2010, Australia

    Contact

  • Sunnybrook Health Sciences Center

    RECRUITING

    Toronto, OH, M4M 3N5, Canada

  • Szpital Wojewdzki w Koszalinie im. Mikoaja Kopernika

    WITHDRAWN

    Koszalin, 75-581, Poland

  • Tampa General Hospital Cancer Institute

    WITHDRAWN

    Tampa, Florida, 33606, United States

  • Texas Onc Methodist (Charlton)

    RECRUITING

    Dallas, Texas, 75237, United States

  • Texas Oncology

    RECRUITING

    Abilene, Texas, 79606-5208, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Texas Oncology - Northeast

    RECRUITING

    Denton, Texas, 76201, United States

  • Texas Oncology Methodist DFW

    RECRUITING

    Dallas, Texas, 75230, United States

  • The Catholic University of Korea, St. Mary's Hospital

    RECRUITING

    Seoul, 06591, South Korea

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • The Chinese University of Hong Kong Prince of Wales Hospital

    RECRUITING

    New Territories, 999077, Hong Kong

  • The Liver Institute at Methodist Dallas Medical Center

    RECRUITING

    Dallas, Texas, 75203, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • The University of Hong Kong

    RECRUITING

    Hong Kong Island, 999077, Hong Kong

  • Tohoku University Hospital

    WITHDRAWN

    Sendai, Miyagi, 980-8574, Japan

  • Tongji University Shanghai East Hospital

    RECRUITING

    Shanghai, China

  • University of California San Diego UCSD - Moores Cancer Center

    RECRUITING

    La Jolla, California, 92093, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Toronto

    RECRUITING

    Toronto, OH, M5G 2M9, Canada

  • West China Hospital- Sichuan University

    RECRUITING

    Chengdu, Sichuan, 610041, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Yonsei University Health System - Severance Hospital

    RECRUITING

    Seoul, 03722, South Korea

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Zhongahan Hospital Fudan unversity

    NOT_YET_RECRUITING

    Shanghai, Shanghai Municipality, 200032, China