Could a ketamine drug ease rett syndrome?

NCT ID NCT06199700

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This early study tested esketamine, a form of ketamine, in 3 girls with Rett syndrome. The goal was to see if weekly infusions over five weeks could improve symptoms and be safe. The trial is complete, but with only 3 participants, it's too small to draw firm conclusions.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Esketamine (a form of ketamine)

What this could lead to

If it works, this could point toward a treatment that eases some symptoms of Rett syndrome.

What could go wrong

This is a very early trial with only 3 participants, so results may not apply to others. Esketamine can cause side effects like high blood pressure or sedation.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Rett syndrome

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Xiamen Children's Hospital (Children's Hospital of Fudan University at Xiamen)

    Xiamen, Fujian, 361006, China