Massive global registry aims to unlock secrets of rett syndrome

NCT ID NCT05432349

First seen Jun 30, 2026 · Last updated Jul 01, 2026 · Updated 1 time

Summary

This study creates a large registry of people with Rett syndrome, a rare genetic disorder that causes severe intellectual and physical disabilities. Researchers will collect information from doctors and caregivers to understand how the disease progresses over time. The goal is to develop better care guidelines and make future clinical trials more effective.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

What this could lead to
If successful, this registry could lead to better care guidelines for Rett syndrome and more effective clinical trials for new treatments.
What could go wrong
This is an observational study, not a treatment trial. It collects data but does not test any therapy, so it won't directly improve symptoms.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

Locations

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Email: •••••@•••••

  • Children's Health

    RECRUITING

    Dallas, Texas, 75207, United States

  • Children's Hospital Colorado

    RECRUITING

    Denver, Colorado, 80045, United States

    Contact Email: •••••@•••••

  • Children's Hospital Los Angeles

    RECRUITING

    Los Angeles, California, 90027, United States

    Contact Email: •••••@•••••

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

  • Gillette Children's Specialty Healthcare

    RECRUITING

    Saint Paul, Minnesota, 55101, United States

    Contact Email: •••••@•••••

  • Greenwood Genetic Center

    RECRUITING

    Greenwood, South Carolina, 29646, United States

  • Kennedy Krieger Institute

    RECRUITING

    Baltimore, Maryland, 21205, United States

    Contact Email: •••••@•••••

  • Nationwide Children's Hospital

    RECRUITING

    Columbus, Ohio, 43205, United States

    Contact Email: •••••@•••••

  • Nicklaus Children's Hospital

    RECRUITING

    Miami, Florida, 33155, United States

    Contact Email: •••••@•••••

  • Rady Children's Hospital - San Diego

    RECRUITING

    San Diego, California, 92123, United States

  • Rush University Medical Center

    RECRUITING

    Chicago, Illinois, 60612, United States

  • Texas Children's Hospital

    RECRUITING

    Houston, Texas, 77030, United States

  • The University of North Carolina at Chapel Hill

    RECRUITING

    Chapel Hill, North Carolina, 27517, United States

  • UCSF Benioff Children's Hospital

    RECRUITING

    Oakland, California, 94598, United States

  • University of Alabama

    RECRUITING

    Birmingham, Alabama, 35233, United States

  • Vanderbilt Kennedy Center

    RECRUITING

    Nashville, Tennessee, 37232, United States

    Contact Email: •••••@•••••

  • Washington University in St. Louis

    RECRUITING

    St Louis, Missouri, 63110, United States

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