New drug may boost blood cell recovery in kids with bone marrow failure

NCT ID NCT06430788

First seen Nov 01, 2025 · Last updated Apr 25, 2026 · Updated 22 times

Summary

This study tests whether giving the drug emapalumab early, before standard treatments, can improve blood cell recovery in children newly diagnosed with severe aplastic anemia. About 35 children will receive emapalumab for up to 6 weeks. The goal is to see if this approach makes standard therapies work better and helps plan the best treatment.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for CYTOPENIA are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Hospital of Philadelphia (Data Collection AND Specimen Analysis)

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Phone: •••-•••-••••

  • Children's Hospital of Wisconsin (Data Collection Only)

    RECRUITING

    Milwaukee, Wisconsin, 53226, United States

    Contact Phone: •••-•••-••••

  • Cincinnati Children's Hospital Medical Center (Data collection only)

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Medical College of Wisconsin (Data Collection AND Data Analysis)

    NOT_YET_RECRUITING

    Milwaukee, Wisconsin, 53226, United States

    Contact Phone: •••-•••-••••

  • Memorial Sloan Kettering Cancer Center (All Protocol Activities)

    RECRUITING

    New York, New York, 10065, United States

    Contact Phone: •••-•••-••••

  • Virginia Commonwealth University (Data Collection Only )

    RECRUITING

    Richmond, Virginia, 23219, United States

    Contact Phone: •••-•••-••••

Conditions

Explore the condition pages connected to this study.