New drug may boost recovery in kids with rare bone marrow failure
NCT ID NCT06430788
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests whether giving emapalumab early can help children with newly diagnosed severe aplastic anemia recover their blood cell counts within 6 weeks. About 35 children will receive the drug before standard treatments. The goal is to see if this approach improves treatment planning and outcomes.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Children's Hospital of Philadelphia (Data Collection AND Specimen Analysis)
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
Contact Phone: •••-•••-••••
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Children's Hospital of Wisconsin (Data Collection Only)
RECRUITINGMilwaukee, Wisconsin, 53226, United States
Contact Phone: •••-•••-••••
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Cincinnati Children's Hospital Medical Center (Data collection only)
RECRUITINGCincinnati, Ohio, 45229, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Medical College of Wisconsin (Data Collection AND Data Analysis)
NOT_YET_RECRUITINGMilwaukee, Wisconsin, 53226, United States
Contact Phone: •••-•••-••••
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Memorial Sloan Kettering Cancer Center (All Protocol Activities)
RECRUITINGNew York, New York, 10065, United States
Contact Phone: •••-•••-••••
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Virginia Commonwealth University (Data Collection Only )
RECRUITINGRichmond, Virginia, 23219, United States
Contact Phone: •••-•••-••••