Cystinosis study probes medication adherence and brain risks
NCT ID NCT02012114
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study looked at 65 people with cystinosis to see how well they take their cysteamine medicine and how that relates to brain problems. Researchers measured medicine use with special bottle caps and diaries, and checked for cystine buildup in the brain using scans and spinal taps. The goal was to understand why some patients develop neurological issues and how to improve treatment.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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Hospices Civils de Lyon
Lyon, 69002, France
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Other studies related to the condition(s) this trial covers.
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