New study maps muscle decline in rare cystinosis patients

NCT ID NCT05545774

First seen Nov 24, 2025 · Last updated May 14, 2026 · Updated 22 times

Summary

This study looked at how cystinosis affects muscles and nerves in 20 patients aged 16 and older. Researchers measured motor function, breathing, swallowing, and sleep over time. The goal was to better understand the disease's progression, not to test a new treatment.

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Contacts and locations

Locations

  • Department of Nephrology and Transplantation Centre de référence des Maladies Rénales Héréditaires de l'Enfant et de l'Adulte, Necker-Enfants Malades University Hospital, APHP

    Paris, France

  • Neurology Department, Raymond-Poincaré hospital, APHP

    Garches, 92380, France

Conditions

Explore the condition pages connected to this study.