New molecules aim to correct cystic fibrosis gene errors in lab tests

NCT ID NCT03670472

Recruiting now Knowledge-focused Sponsor: University Hospital, Lille Source: ClinicalTrials.gov ↗

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study looks at whether certain molecules can fix nonsense mutations in the CFTR gene, which cause cystic fibrosis. Researchers will take cells from the noses of 85 people with cystic fibrosis and test different molecules to see which ones can restore the function of the CFTR protein. The goal is to learn which mutations can be corrected and how, paving the way for future treatments.

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Conditions

The condition(s) this trial relates to.

cystic fibrosis

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

CYSTIC FIBROSIS

Contacts and locations

Locations

Aphm Hopital La Timone - Marseille
RECRUITING

Marseille, France
Camsp Chu Amiens
RECRUITING

Amiens, France
Chu Montpellier
RECRUITING

Montpellier, France
Cmp Enfants Aphp Robert Debre - Paris
RECRUITING

Paris, France
Hopital Femme Mere Enfant - Hcl - Bron
RECRUITING

Bron, France
Hopitaux Universitaires de Strasbour
RECRUITING

Strasbourg, France
Hu Paris Centre Site Cochin Aphp - Paris 14
RECRUITING

Paris, France
Hôpital Calmette,CHU
RECRUITING

Lille, France

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