Engineered immune cells take on rare blood disorders

NCT ID NCT07603557

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 2 times

Summary

This phase 2 trial tests a personalized CAR T cell therapy called zolacabtagene autoleucel in 52 adults with chronic immune thrombocytopenia (ITP) or autoimmune hemolytic anemia (AIHA). The treatment uses the patient's own immune cells, modified to target and destroy faulty B cells that attack blood cells. The study aims to see if this approach can safely improve blood counts and reduce symptoms.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

zolacabtagene autoleucel (a CAR T cell therapy made from the patient's own immune cells)

What this could lead to

If it works, this could offer a new treatment option for people with chronic ITP or AIHA who have not responded to other therapies, potentially reducing the need for ongoing medication.

What could go wrong

This is an early phase 2 trial with only 52 participants, so results may not apply to everyone. CAR T cell therapy can cause serious side effects like cytokine release syndrome and neurological problems.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

autoimmune hemolytic anemia autoimmune thrombocytopenic purpura

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

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Locations

  • Local Institution - 101

    Boston, Massachusetts, 02114, United States

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  • Local Institution - 102

    Seattle, Washington, 98109, United States

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  • Local Institution - 103

    Houston, Texas, 77030-2740, United States

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  • Local Institution - 201

    Odense, DK-5000, Denmark

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  • Local Institution - 301

    Magdeburg, Saxony-Anhalt, 39120, Germany

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  • Local Institution - 302

    Erlangen, 91054, Germany

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  • Local Institution - 401

    London, Greater London, W12 OHS, United Kingdom

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  • Local Institution - 402

    Sheffield, S10 2SJ, United Kingdom

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