New drug BTX-A51 tested in rare sarcomas

NCT ID NCT06414434

First seen Jun 25, 2026 · Last updated Jul 01, 2026 · Updated 3 times

Summary

This early study tests an oral drug called BTX-A51 in 24 people with advanced liposarcoma (a type of fat tissue cancer) that has spread or come back. The main goal is to see if the drug is safe and tolerable at different doses. It focuses on specific genetic subtypes: MDM2-amplified, myxoid, and CIC-rearranged sarcomas.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

BTX-A51 (a kinase inhibitor taken orally)

What this could lead to

If it works, this could point toward a new treatment option for certain types of liposarcoma that have spread or come back.

What could go wrong

This is a very early (Phase 1) pilot study with only 24 people, so it is primarily checking safety and dosing. It may not show strong anti-cancer effects, and side effects are unknown.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

CIC-rearranged sarcoma dedifferentiated liposarcoma liposarcoma myxoid liposarcoma well-differentiated liposarcoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Brigham and Women's Hospital

    Boston, Massachusetts, 02215, United States

  • Dana-Farber Cancer Institute

    Boston, Massachusetts, 02215, United States