New drug trial hopes to tame rare genetic heart disease

NCT ID NCT07241104

First seen Nov 21, 2025 · Last updated Apr 28, 2026 · Updated 22 times

Summary

This early-stage study tests a new medicine called AZD4063 in 31 adults with a specific genetic heart condition (PLN R14del dilated cardiomyopathy). The main goal is to check if the drug is safe and how the body processes it. Participants must have a weakened heart pump and be on stable heart medications.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Research Site

    NOT_YET_RECRUITING

    Amsterdam, 1081 HV, Netherlands

  • Research Site

    RECRUITING

    Groningen, 9713 GZ, Netherlands

  • Research Site

    RECRUITING

    Rotterdam, 3015 GD, Netherlands

  • Research Site

    RECRUITING

    Utrecht, 3584 CX, Netherlands

Conditions

Explore the condition pages connected to this study.