New combo therapy targets Hard-to-Treat cancers with genetic marker

NCT ID NCT06360354

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This early-stage trial is testing a new drug called anvumetostat, given together with other standard chemotherapy drugs, for people with advanced cancers of the digestive system (stomach, bile ducts, or pancreas) that have a specific genetic change called MTAP deletion. The main goals are to find the safest dose and to check for side effects. About 120 adults will take part.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Anvumetostat (AMG 193) combined with gemcitabine, nab-paclitaxel, modified FOLFIRINOX, or RMC-6236

What this could lead to

If successful, this could point toward a new treatment option for people with certain hard-to-treat digestive cancers that have a specific genetic marker.

What could go wrong

This is an early Phase 1b trial with only 120 participants, so it is primarily testing safety and dosing. It is too soon to know if the combination will work, and there may be side effects from the drugs.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

neoplasm pancreatic adenocarcinoma pancreatic neoplasm

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Aichi Cancer Center

    Nagoya, Aichi-ken, 464-8681, Japan

  • Alexandra Hospital

    Athens, 11528, Greece

  • Arthur J E Child Comprehensive Cancer Centre

    Calgary, Alberta, T2N 5G2, Canada

  • Austin Health, Austin Hospital

    Heidelberg, Victoria, 3084, Australia

  • Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda

    Milan, 20162, Italy

  • Beth Israel Deaconess Medical Center

    Boston, Massachusetts, 02215, United States

  • CHU de Quebec Hopital de l Enfant Jesus

    Québec, Quebec, G1J 1Z4, Canada

  • Centre Georges Francois Leclerc

    Dijon, 21000, France

  • Centro Ricerche Cliniche Di Verona Societa responsabilita limitata

    Verona, 37134, Italy

  • Chris OBrien Lifehouse

    Camperdown, New South Wales, 2050, Australia

  • City of Hope National Medical Center

    Duarte, California, 91010, United States

  • City of Hope Orange County Lennar Foundation Cancer Center

    Duarte, California, 91010, United States

  • Cleveland Clinic Foundation

    Cleveland, Ohio, 44195, United States

  • Comprehensive Blood and Cancer Center

    Bakersfield, California, 93309, United States

  • Comprehensive Cancer Centers of Nevada

    Las Vegas, Nevada, 89169, United States

  • Dana-Farber Cancer Institute

    Boston, Massachusetts, 02215, United States

  • Duke University

    Durham, North Carolina, 27710, United States

  • Epworth Healthcare

    St Albans, Victoria, 3021, Australia

  • European Interbalkan Medical Center

    Thessaloniki, 57001, Greece

  • Fondazione IRCCS Istituto Nazionale dei Tumori

    Milan, 20133, Italy

  • Fred Hutchinson Cancer Center

    Seattle, Washington, 98106, United States

  • General Hospital Of Thessaloniki Papageorgiou

    Thessaloniki, 56429, Greece

  • GenesisCare -North Shore Oncology

    St Leonards, New South Wales, 2065, Australia

  • Gustave Roussy

    Villejuif, 94805, France

  • Harbin Medical University Cancer Hospital

    Harbin, Heilongjiang, 150000, China

  • Hartford Hospital

    Hartford, Connecticut, 06106, United States

  • Herlev og Gentofte Hospital

    Herlev, 2730, Denmark

  • Hospital General Universitario Gregorio Maranon

    Madrid, 28009, Spain

  • Hospital Universitari Vall d Hebron

    Barcelona, Catalonia, 08035, Spain

  • Hospital Universitario Virgen del Rocio

    Seville, Andalusia, 41013, Spain

  • IRCCS Istituto Clinico Humanitas

    Rozzano MI, 20089, Italy

  • Indiana University

    Indianapolis, Indiana, 46202, United States

  • Institut Bergonie

    Bordeaux, 33000, France

  • Institut Paoli Calmettes

    Marseille, 13009, France

  • Kanagawa Prefectural Hospital Organization Kanagawa Cancer Center

    Yokohama, Kanagawa, 241-8515, Japan

  • Memorial Sloan Kettering Cancer Center

    New York, New York, 10065, United States

  • Mengchao Hepatobiliary Hospital of Fujian Medical University

    Fuzhou, Fujian, 350028, China

  • National Cancer Center Hospital

    Chuo-ku, Tokyo, 104-0045, Japan

  • National Cancer Center Hospital East

    Kashiwa-shi, Chiba, 277-8577, Japan

  • National Cheng Kung University Hospital

    Tainan, 70403, Taiwan

  • National Taiwan University Hospital

    Taipei, 10002, Taiwan

  • Northwest Cancer Specialists - Vancouver

    Vancouver, Washington, 98684, United States

  • Northwest Medical Specialties, PLLC

    Tacoma, Washington, 98405, United States

  • Norton Cancer Institute

    Louisville, Kentucky, 40202, United States

  • Norwalk Hospital

    Norwalk, Connecticut, 06856, United States

  • Oncology Consultants Cancer Center

    Houston, Texas, 77030, United States

  • Peter MacCallum Cancer Centre

    Melbourne, Victoria, 3000, Australia

  • Prince of Wales Hospital, Chinese University of Hong Kong

    Shatin, New Territories, Hong Kong

  • Princess Margaret Cancer Centre

    Toronto, Ontario, M5G 1Z5, Canada

  • Queen Elizabeth Hospital Birmingham

    Birmingham, B15 2TH, United Kingdom

  • Queen Mary Hospital, The University of Hong Kong

    Hong Kong, Hong Kong

  • Radboud Universitair Medisch Centrum

    Nijmegen, 6525 GA, Netherlands

  • Rocky Mountain Cancer Centers

    Aurora, Colorado, 80012, United States

  • Sarah Cannon Research Institute UK

    London, W1G 6AD, United Kingdom

  • Sun Yat-Sen University Cancer Center

    Guangzhou, Guangdong, 510030, China

  • Taipei Veterans General Hospital

    Taipei, 11217, Taiwan

  • The First Affiliated Hospital of Zhengzhou University

    Zhengzhou, Henan, 450052, China

  • The First Bethune Hospital of Jilin University

    Changchun, Jilin, 130021, China

  • The Queen Elizabeth Hospital

    Woodville South, South Australia, 5011, Australia

  • Translational Research in Oncology US Inc, Trio Central Pharmacy

    Los Angeles, California, 90095, United States

  • US Oncology Research Investigational Products Center

    Irving, Texas, 75063, United States

  • Union Hospital Tongji Medical College Huazhong University of Science and Technology

    Wuhan, Hubei, 430022, China

  • United States Oncology Regulatory Affairs Corporate Office

    Nashville, Tennessee, 37203, United States

  • Universitaetsklinikum Essen

    Essen, 45147, Germany

  • Universitaetsklinikum Heidelberg

    Heidelberg, 69120, Germany

  • Universitaetsklinikum Wuerzburg

    Würzburg, 97078, Germany

  • Universitair Ziekenhuis Antwerpen

    Edegem, 2650, Belgium

  • Universitair Ziekenhuis Leuven - Campus Gasthuisberg

    Leuven, 3000, Belgium

  • Universite Catholique de Louvain Cliniques Universitaires Saint Luc

    Brussels, 1200, Belgium

  • University of California Los Angeles

    Santa Monica, California, 90404, United States

  • University of California San Diego Moores Cancer Center

    La Jolla, California, 92093, United States

  • University of Chicago

    Chicago, Illinois, 60637, United States

  • University of Nebraska

    Omaha, Nebraska, 68198, United States

  • University of Virginia Cancer Center

    Charlottesville, Virginia, 22903, United States

  • Virginia Cancer Specialists PC

    Fairfax, Virginia, 22031, United States

  • Washington University

    St Louis, Missouri, 63110, United States

  • Yale University

    New Haven, Connecticut, 06520, United States