New RNA drug shows promise in preventing HAE attacks in ongoing study

NCT ID NCT07428499

First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 2 times

Summary

This study is for people with hereditary angioedema (HAE) who have already completed a previous trial of the drug ADX-324. ADX-324 is an RNA-based medicine designed to lower a protein involved in swelling attacks. The goal is to see if long-term use is safe and can reduce the number of attacks. About 90 participants will receive additional doses of ADX-324 and be monitored for side effects and attack frequency.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ADX-324 (a type of RNA drug called siRNA that targets prekallikrein)

What this could lead to

If successful, ADX-324 could offer a new way to prevent painful swelling attacks in people with hereditary angioedema, reducing attack frequency and improving quality of life.

What could go wrong

This is an extension study, so participants already tolerated the drug, but long-term safety and effectiveness are still being checked. HAE attacks may still occur, and the drug may not work for everyone.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

hereditary angioedema hereditary angioedema type 1 hereditary angioedema type 2

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Litchfield Park, Arizona, 85340, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Little Rock, Arkansas, 72205, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    San Diego, California, 92122, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Walnut Creek, California, 94598, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Orlando, Florida, 32807, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Chevy Chase, Maryland, 20815, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Wheaton, Maryland, 20902, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Detroit, Michigan, 48202, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    St Louis, Missouri, 63141, United States

  • ADARx Clinical Site

    RECRUITING

    Las Vegas, Nevada, 89128, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    New York, New York, 10029, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Cincinnati, Ohio, 45236, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Columbus, Ohio, 43235, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Toledo, Ohio, 43617, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Hershey, Pennsylvania, 17033, United States

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Capital Federal, Buenos Aires, C1425BEN, Argentina

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Buenos Aires, Buenos Aires F.D., C1035AAT, Argentina

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Adelaide, South Australia, 5000, Australia

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Vienna, 1090, Austria

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Edegem, Antwerpen, 2650, Belgium

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Sofia, 1000, Bulgaria

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Edmonton, Alberta, T6G 2R3, Canada

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Ottawa, Ontario, K1H 1E4, Canada

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Montreal, Quebec, H2W 1R7, Canada

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Beijing, 100730, China

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Harbin, 150001, China

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Zhengzhou, 450003, China

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Split, 21000, Croatia

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Zagreb, 10000, Croatia

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Hradec Králové, 500 05, Czechia

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Prague, 15000, Czechia

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Nice, Alpes-Maritimes, 06300, France

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Tours, Indre-et-Loire, 37000, France

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Montpellier, 34295, France

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Paris, 75012, France

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Tübingen, Baden-Wurttemberg, 72076, Germany

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Hong Kong, 111, Hong Kong

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Budapest, 1088, Hungary

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Ashkelon, 7830604, Israel

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Tel Aviv, 5262100, Israel

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Lodz, 92-213, Poland

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Barcelona, 08907, Spain

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Madrid, 28007, Spain

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Taichung, 40705, Taiwan

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Cambridge, CB2 0QQ, United Kingdom

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Cardiff, CF14 4YS, United Kingdom

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    London, E1 1BB, United Kingdom

  • ADARx Clinical Site

    NOT_YET_RECRUITING

    Southampton, SO16 6YD, United Kingdom