Experimental drug ACT001 targets tough brain tumors in small trial

NCT ID NCT06894225

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This phase 2 trial is testing an oral drug called ACT001 in 12 adults whose glioblastoma has returned after standard treatment. The study focuses on patients whose tumors have a specific genetic signature (STAT3-high). Researchers will check if the drug can shrink or stabilize the tumor for at least 24 weeks. The trial is currently suspended.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ACT001 (a drug taken orally twice daily)

What this could lead to

If successful, this could point toward a new treatment option for patients with recurrent glioblastoma who have a specific genetic marker.

What could go wrong

This is a very small, early-phase trial with only 12 participants, and it is currently suspended. The drug may not shrink tumors or improve survival, and side effects are possible.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

glioblastoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • National Neuroscience Institute

    Singapore, Singapore