Gene therapy trial aims to halt vision loss in rare inherited eye disease
Disease control
Recruiting now
This study is testing a gene therapy called AAV5-hRKp.RPGR to see if it is safe and can help preserve or improve vision in Japanese patients with a specific, inherited form of retinitis pigmentosa (XLRP). The therapy involves a one-time injection into the back of both eyes to del…
Phase: PHASE3 • Sponsor: Janssen Pharmaceutical K.K. • Aim: Disease control
Last updated Apr 01, 2026 14:43 UTC