Experimental gene therapy targets rare blindness in japanese patients

NCT ID NCT05926583

First seen Nov 01, 2025 · Last updated Apr 29, 2026 · Updated 30 times

Summary

This study tests a gene therapy for a rare inherited eye disease called X-linked retinitis pigmentosa, which causes gradual vision loss. The treatment delivers a working gene to the retina using a harmless virus. The study involves 4 Japanese participants aged 5 or older and focuses on safety and whether it can slow vision decline.

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Contacts and locations

Locations

  • National Hospital Organization Tokyo Medical Center

    Meguro-ku, 1528902, Japan

Conditions

Explore the condition pages connected to this study.