Gene therapy trial offers hope for rare blindness condition

NCT ID NCT05926583

First seen Nov 01, 2025 · Last updated Jun 16, 2026 · Updated 35 times

Summary

This study tests a gene therapy for Japanese people with X-linked retinitis pigmentosa, an inherited eye disease that causes vision loss. The treatment uses a harmless virus to deliver a working gene to the retina. The main goal is to check safety, with a secondary focus on whether it improves vision in low light after one year.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • National Hospital Organization Tokyo Medical Center

    Meguro-ku, 1528902, Japan

Conditions

The condition(s) this trial relates to.

retinitis pigmentosa

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.