First-in-Human cell therapy tested for rare muscle disease
Disease control
Completed
This early-stage study tested the safety of a new cell therapy called MuSK-CAART in seven people with a rare autoimmune disease that causes severe muscle weakness. Researchers gave different doses, sometimes with other medications, to see how the body handled the treatment. The g…
Phase: PHASE1 • Sponsor: Cabaletta Bio • Aim: Disease control
Last updated Mar 30, 2026 14:30 UTC