Baxalta Now Part Of Shire

This early-stage study tested a single intravenous infusion of an experimental gene therapy called BAX 888 in adult men with severe hemophilia A. The main goals were to check for side effects and find a safe and effective dose. Researchers hoped the therapy would help the body pr…

This study tested the long-term safety and effectiveness of a replacement therapy called rVWF (vonicog alfa) for people with severe von Willebrand disease (VWD), a disorder that prevents blood from clotting properly. The main goal was to see how well regular, preventive infusions…

This study tested a new medicine called BAX 930 for people born with a severe, inherited blood clotting disorder called congenital TTP. The goal was to see if BAX 930, which replaces a missing enzyme, could prevent or treat dangerous clotting events better than the standard treat…