Three-Year trial tests new therapy to prevent dangerous bleeds

NCT ID NCT03879135

Summary

This study tested the long-term safety and effectiveness of a replacement therapy called rVWF (vonicog alfa) for people with severe von Willebrand disease (VWD), a disorder that prevents blood from clotting properly. The main goal was to see how well regular, preventive infusions of this therapy could reduce the rate of spontaneous bleeding episodes over time. The study followed 38 participants, including children and adults, for up to three years to monitor their bleeding rates and any side effects from the treatment.

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Contacts and locations

Locations

  • AKH - Medizinische Universität Wien

    Vienna, Austria

  • Arkansas Children's Hospital Research Institute

    Little Rock, Arkansas, 72202, United States

  • Azienda Ospedaliera Pediatrica Santobono Pausillipon

    Naples, Italy

  • Azienda Ospedaliera Universitaria Careggi

    Florence, 50134, Italy

  • Azienda Ospedaliera Universitaria Policlinico Umberto I - Università di Roma La Sapienza

    Roma, 00185, Italy

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Ege University Medical Faculty

    Izmir, 35040, Turkey (Türkiye)

  • Ege University Medical Faculty

    Izmir, 35100, Turkey (Türkiye)

  • Erasmus Medisch Centrum

    Rotterdam, 3015 AA, Netherlands

  • Erasmus Medisch Centrum

    Rotterdam, 3015 CN, Netherlands

  • FSBI of Science "Kirov Scientific and Research Institute of Hematology and Blood Transfusion of FMBA

    Kirov, 610017, Russia

  • Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico

    Milan, Italy

  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS

    Roma, 00168, Italy

  • Groupe Hospitalier Pellegrin - Hôpital Pellegrin

    Gironde, France

  • Groupement Hospitalier Est- Hôpital Louis Pradel

    Bron, 69677, France

  • Groupement Hospitalier Sud - Hôpital Bicêtre

    Le Kremlin-Bicêtre, 94270, France

  • Hopital Cardiologique - CHU Lille

    Lille, Nord, France

  • Hospital General Universitario de Alicante

    Alicante, 03010, Spain

  • Hospital Universitari i Politecnic La Fe

    Valencia, 46026, Spain

  • Hospital Universitario La Paz

    Madrid, 28046, Spain

  • Hôpital Necker - Enfants Malades

    Paris, Paris, 75015, France

  • Indiana Hemophilia and Thrombosis Center

    Indianapolis, Indiana, 46260, United States

  • Istanbul University Oncology Institute

    Istanbul, Turkey (Türkiye)

  • Klinikum der Johann Wolfgang Goethe-Universitaet

    Frankfurt, Germany

  • Medical University of South Carolina (MUSC)

    Charleston, South Carolina, 29425, United States

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Ondokuz Mayis Univ. Med. Fac.

    Samsun, 55139, Turkey (Türkiye)

  • Ospedale Pediatrico Bambino Gesù

    Roma, Italy

  • Rainbow Babies and Children's Hospital

    Cleveland, Ohio, 44106, United States

  • SAIH "Kemerovo Regional Clinical Hospital"

    Kemerovo, 650066, Russia

  • University of Colorado Health

    Aurora, Colorado, 80045, United States

  • University of Florida College of Medicine

    Gainesville, Florida, 32610, United States

  • Werlhof-Institut GmbH

    Hanover, Germany

Conditions

Explore the condition pages connected to this study.