Baxalta Now Part Of Shire
Clinical trials sponsored by Baxalta Now Part Of Shire, explained in plain language.
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One-Shot gene therapy aims to free hemophilia patients from lifelong injections
⭐️ CURE ⭐️ OngoingThis early-stage trial is testing a single injection of gene therapy for adults with hemophilia B. The goal is to see if the treatment is safe and if it can help the body produce its own missing clotting factor, potentially reducing or eliminating the need for regular injections.…
Phase: PHASE1, PHASE2 • Sponsor: Baxalta now part of Shire • Aim: ⭐️ CURE ⭐️
Last updated Mar 27, 2026 12:39 UTC
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Scientists track long-term safety of advanced hemophilia drug
Disease control OngoingThis study is monitoring the long-term safety of ADYNOVI/ADYNOVATE, a medication for hemophilia A, in 207 patients who are already using it as part of their regular care. The main goal is to check for any side effects that might develop over time, especially those affecting the k…
Sponsor: Baxalta now part of Shire • Aim: Disease control
Last updated Mar 30, 2026 14:27 UTC