New shot aims to slash dangerous cholesterol in teens with rare genetic disease
Disease control
Not yet recruiting
This study tests an experimental drug called zodasiran in 12 teenagers (ages 12 to 17) with homozygous familial hypercholesterolemia, a rare genetic condition causing extremely high cholesterol. Participants receive injections of zodasiran to see if it safely lowers their LDL cho…
Phase: PHASE3 • Sponsor: Arrowhead Pharmaceuticals • Aim: Disease control
Last updated May 17, 2026 05:07 UTC