SMA
Clinical trials for SMA explained in plain language.
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New drug hopes to boost muscle power in babies with SMA
Disease control Recruiting nowThis study tests a drug called apitegromab in children under 2 years old who have spinal muscular atrophy (SMA), a genetic condition that causes muscle weakness. The drug works by blocking a protein that limits muscle growth. Researchers want to see if adding apitegromab to stand…
Matched conditions: SMA
Phase: PHASE2 • Sponsor: Scholar Rock, Inc. • Aim: Disease control
Last updated Jun 27, 2026 12:28 UTC
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Swiss launch major registry to track rare muscle diseases
Knowledge-focused Recruiting nowThis study is a registry that collects health information from people in Switzerland who have neuromuscular disorders like SMA, DMD, BMD, and others. It aims to track symptoms, treatments, and outcomes over time to help researchers and doctors improve care. No new treatments are …
Matched conditions: SMA
Sponsor: University of Bern • Aim: Knowledge-focused
Last updated Jun 27, 2026 08:11 UTC