PNH
Clinical trials for PNH explained in plain language.
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New drug shows promise in controlling rare blood disorder
Disease control CompletedThis completed Phase 3 study tested whether the drug ravulizumab could effectively control paroxysmal nocturnal hemoglobinuria (PNH), a rare and serious blood disease, in Chinese adults who hadn't previously tried this type of medication. The trial involved 18 participants and me…
Matched conditions: PNH
Phase: PHASE3 • Sponsor: Alexion Pharmaceuticals, Inc. • Aim: Disease control
Last updated Mar 31, 2026 12:12 UTC
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Oral pill challenge to injection for rare blood disease shows promise
Disease control CompletedThis completed Phase 3 trial tested if a new oral tablet called HSK39297 could work as well as the standard injected drug (eculizumab) for people with a rare blood disease called PNH who had never tried this type of medicine before. The main goal was to see if the pill could safe…
Matched conditions: PNH
Phase: PHASE3 • Sponsor: Haisco Pharmaceutical Group Co., Ltd. • Aim: Disease control
Last updated Mar 30, 2026 14:28 UTC