New hope for PNH patients: Long-Term drug safety trial underway
NCT ID NCT03531255
First seen Apr 08, 2026 · Last updated May 12, 2026 · Updated 5 times
Summary
This study looks at the long-term safety and effectiveness of pegcetacoplan in people with PNH, a rare blood disorder. Participants must have completed a prior pegcetacoplan study and shown benefit. The main goal is to track side effects over time.
Disclaimer
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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AZ Delta
Roeselare, 8800, Belgium
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Acibadem City Clinic Tokuda Hospital
Sofia, 1407, Bulgaria
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Alberta Health Services
Edmonton, Alberta, T6G 2V2, Canada
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Baptist Cancer Center
Memphis, Tennessee, 38120, United States
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CHRU de Lille
Lille, 59037, France
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Cancer Specialists of North Florida
Jacksonville, Florida, 32257, United States
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Centre Hospitalier Annecy Genevois - Site Annecy
Pringy, 74374, France
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Centre Hospitalier de Saint-Quentin
Saint-Quentin, 02321, France
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Centro de Investigacion en Hematologia Clinica del Centro Medico Corpac
San Isidro, Lima region, 15047, Peru
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Chungnam National University Hospital
Junggu, Daejeon, 35015, South Korea
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Cleveland Clinic
Cleveland, Ohio, 44195, United States
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Clinical Center of Serbia
Belgrade, 11000, Serbia
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Cliniques Universitaires Saint-luc
Brussels, 1200, Belgium
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Denver Health Medical Center
Denver, Colorado, 80204, United States
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Duke University Medical Center
Durham, North Carolina, 27710, United States
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Essen University Hospital Department of Hematology
Essen, North Rhine-Westphalia, 45147, Germany
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Hopital Saint-Louis
Paris, 75010, France
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Hospital Ampang
Ampang, Selangor, 68000, Malaysia
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Hospital Center Chalon Sur Saone William Morey
Chalon-sur-Saône, 71100, France
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Hospital Edgardo Rebagliatti
Jesús María, Lima, 15072, Peru
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Hospital Nacional Dos De Mayo - Centro de Investigación
Lima Cercado, Lima region, 15003, Peru
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Hospital Univ. de Gran Canaria Dr.Negrin
Las Palmas de Gran Canaria, Canary Islands, 35019, Spain
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Hospital Universitario "José Eleuterio González", UANL
Monterrey, 64460, Mexico
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Hospital Universitario Politecnico La Fe
Valencia, 46026, Spain
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IPS Centro Medico Julian Coronel SAS
Cali, Valle del Cauca Department, 760035, Colombia
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Investigative Clinical Research of Indiana
Indianapolis, Indiana, 46260, United States
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Japanese Red Cross Nagoya Daini Hospital
Showa-ku, Aichi-ken, 486-8650, Japan
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Juntendo University Hospital
Bunkyō-Ku, Tokyo, 113-8421, Japan
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Kinan Hospital
Tanabe, Wakayama, 646-8588, Japan
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Lakes Research
Miami, Florida, 33014, United States
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Leeds Teaching Hospitals NHS Trust
Leeds, LS9 7TF, United Kingdom
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Lyon Sud Hospital Center
Pierre-Bénite, 69495, France
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Maharaj Nakorn Chiang Mai Hospital
Chiang Mai, 50200, Thailand
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Makati Medical Centre
Makati City, National Capital Region, 1229, Philippines
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Mary Mediatrix Medical Centre
Lipa City, National Capital Region, 4217, Philippines
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NTT Medical Center Tokyo
Tokyo, 141-0022, Japan
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National Specialized Hospital for Active Treatment of Haematologic Diseases
Sofia, 1756, Bulgaria
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Northwestern University
Chicago, Illinois, 60611, United States
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Okayama University Hospital
Okayama, 700-8558, Japan
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Pavlov First Saint Petersburg State Medical University
Saint Petersburg, 197022, Russia
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Perpetual Succour Hospital
Cebu, National Capital Region, 6000, Philippines
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Phramongkutklao Hospital
Bangkok, 10400, Thailand
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Prince of Wales Hospital
Hong Kong, Hong Kong
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Queen Mary Hospital
Hong Kong, Hong Kong
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Ramathibodi Hospital
Bangkok, 10400, Thailand
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Royal Melbourne Hospital
Melbourne, Victoria, 3000, Australia
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Shinshu University Hospital
Matsumoto, Nagano, 390-8621, Japan
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Singapore General Hospital
Singapore, 169608, Singapore
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Siriraj Hospital
Bangkok, 10400, Thailand
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Songklanagarind Hospital
Songkhla, 90110, Thailand
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Srinagarind Hospital
Khon Kaen, 40002, Thailand
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St. Lukes Medical Centre
Quezon City, National Capital Region, 1112, Philippines
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Thammasat University Hospital
Pathum Thani, 12120, Thailand
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The Medical City
Pasig, National Capital Region, 1604, Philippines
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Therapeutic hospital of regional clinical hospital #1
Tyumen, 625023, Russia
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Toronto General Hospital
Toronto, Ontario, M5G 2C4, Canada
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Uniklinik RWTH Aachen
Aachen, North Rhine-Westphalia, 52074, Germany
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Universitatsklinikum Ulm
Ulm, Baden-Wurttemberg, 89081, Germany
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University Malaya Medical Centre
Lembah Pantai, Kuala Lumpur, 59100, Malaysia
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University Medical Center Hamburg-Eppendorf
Hamburg, 20246, Germany
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University of Calgary
Calgary, Alberta, T2N 4Z6, Canada
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University of Southern California
Los Angeles, California, 90033, United States
Conditions
Explore the condition pages connected to this study.