PHENYLKETONURIA
Clinical trials for PHENYLKETONURIA explained in plain language.
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New pill for PKU shows promise in early human testing
Disease control CompletedThis early-stage study tested an experimental oral drug called JNT-517 in healthy volunteers and people with phenylketonuria (PKU), a genetic condition that causes harmful buildup of the amino acid phenylalanine. The main goals were to check safety and how the body processes the …
Matched conditions: PHENYLKETONURIA
Phase: PHASE1, PHASE2 • Sponsor: Otsuka Pharmaceutical Development & Commercialization, Inc. • Aim: Disease control
Last updated Jun 27, 2026 12:29 UTC
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Could a probiotic pill help kids with PKU?
Disease control CompletedThis study tested an engineered probiotic called CBT102-A in 15 children with phenylketonuria (PKU), a condition where the body cannot break down an amino acid called phenylalanine. The children took the probiotic or a placebo for 20 days. The goal was to see if the probiotic cou…
Matched conditions: PHENYLKETONURIA
Phase: EARLY_PHASE1 • Sponsor: Children's Hospital of Fudan University • Aim: Disease control
Last updated Jun 27, 2026 09:08 UTC
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PKU patients may have hidden inflammation, study suggests
Knowledge-focused CompletedThis study looked at 40 adults—some with phenylketonuria (PKU) and some healthy—to see if PKU causes low-level inflammation in the body. Researchers measured inflammatory markers in blood samples. The goal was to better understand how PKU affects overall health, not to test a new…
Matched conditions: PHENYLKETONURIA
Phase: NA • Sponsor: University Hospital, Tours • Aim: Knowledge-focused
Last updated Jun 27, 2026 08:06 UTC